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Therapies
7 recordsAntisense Oligonucleotides · Antisense oligonucleotides
Short synthetic nucleic-acid strands designed to bind a selected RNA sequence and alter its processing or use.
Enzyme Replacement therapy · Enzyme replacement therapy
Treatment with a manufactured enzyme to replace or supplement activity that is deficient in a particular disease.
siRNA Therapeutics · siRNA therapeutics
Short double-stranded RNAs that guide cellular RNA-interference machinery to a complementary target RNA.
SOD1-targeted Antisense research · SOD1-targeted antisense research
An example of using an antisense drug to reduce RNA from a disease-associated gene rather than inhibit its protein product.
Substrate Reduction therapy · Substrate reduction therapy
A strategy that lowers production of a material that accumulates when its breakdown pathway is impaired.
Therapeutic Antibodies · Therapeutic antibodies
Medicines made from antibodies that recognize targets such as receptors, soluble proteins, or cell-surface markers.
Vaccination
An intervention that presents antigenic information to the immune system to help establish protective responses and memory.